Fighting rare diseases
In the UK, there are thousands of children living with a rare and life-limiting disease for which there is no cure.
Children like Danny who has the rare disease, Hunter syndrome. Danny’s family are painfully aware that time with their youngest son will be cruelly cut short by this disease.
“We will lose our beautiful boy to Hunter syndrome,” says mum Sally. “But any new hope is worth fighting for. So that families in the future don’t have to feel that the bottom is dropping out of their world.”
Help fund vital research – together we can bring hope to families fighting rare and incurable diseases.
Other appeals
Transforming babies’ lives
Help to fund research that could revolutionise screening of newborn babies for cytomegalovirus (CMV) – allowing early detection and treatment that can protect babies from the devastating consequences of this virus.
Searching for a new treatment
Help fund an urgently needed piece of research that could lead to a new treatment to improve the outlook for children fighting Vici syndrome - a devastating rare disease that can severely shorten children’s lives, with many not living beyond their fifth birthday.
Fighting premature birth
Over 1,000 babies die each year in the UK due to premature birth. Globally, it’s the biggest killer of children under 5. Join the fight for babies born too soon. Together we will find the answers.