Fighting rare diseases
In the UK, there are thousands of children living with a rare and life-limiting disease for which there is no cure.
Children like Danny who has the rare disease, Hunter syndrome. Danny’s family are painfully aware that time with their youngest son will be cruelly cut short by this disease.
“We will lose our beautiful boy to Hunter syndrome,” says mum Sally. “But any new hope is worth fighting for. So that families in the future don’t have to feel that the bottom is dropping out of their world.”
Help fund vital research – together we can bring hope to families fighting rare and incurable diseases.
Other appeals
Fighting a rare brain disease
Help fund a cutting-edge piece of research that could improve the outlook for children fighting a rare brain disease, called NMDAR-antibody encephalitis. A disease that can have a devastating impact on young lives.
Unlocking new epilepsy treatments
Thousands of children in the UK suffer from epilepsy that can have devastating effects on young lives. That’s why we urgently need your help to fund research that could unlock vital new treatments for children living with epilepsy.
Help protect preterm babies
This Christmas, support vital research that could help premature babies fight life-threatening infections in their critical first weeks of life, helping to save lives and reduce life-changing complications.
COVID-19 Children's Research Appeal
We need your help to fund research to better understand how COVID-19 affects babies, children and young people and help tackle COVID-19 in children.