Rare diseases
Thousands of families across the UK are coping with the challenge of caring for children with rare and devastating diseases for which there are no cures.
Lily is living with BPAN, a rare and devastating neurological condition for which there is no cure.
This disease strikes young children, causing them to develop slowly. It leads to seizures, muscle problems, symptoms of Parkinson's, dementia and eventually early death.
Current Research
We’re giving her the best time we can while she’s here
Previous Research
Ways to support our work
Donate online
Your donation to Action Medical Research can help save and change children's lives.
Volunteering
Volunteers are essential to what we do. We would be very appreciative of your help across a number of important roles.
Fundraise for us
We have funded some amazing breakthroughs but we want to do more. You can help by fundraising for us!
Events
At Action Medical Research, we offer some incredible charity events whatever your ambitions, sporting ability or location.